Advancing Integrated Therapies for Gaucher Disease

Advancing Integrated Therapies for Gaucher Disease: Neuronopathic Innovation and Combination Strategies for Refractory Skeletal Disease

Overview

ClinicalTrials.gov ID: NCT07758816
Lead Sponsor: Yale UniversityOTHER
Brief Summary: The purpose of this study is to better understand the natural history, clinical outcomes, and biological features of Gaucher disease in patients receiving standard medical care
Study Type: Observational

Phase

No data available

Enrollment

30Estimated

Conditions

Gaucher Disease

Interventions

No data available

Organization Study ID

2000042004

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