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Individual patient expanded access requests may be considered for patients who have no other treatment options.
Expanded access may provide access for treatment prior to approval by the local regulatory agency.
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| Name | Type | Description | Arm Group Labels | Other Names |
|---|---|---|---|---|
| Velmanase Alfa | Drug |
|
Inclusion Criteria:
-
Exclusion Criteria:
-
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| Name | Role | Phone | Extension | |
|---|---|---|---|---|
| Expanded Access | Contact | (888) 661-9260 | GRD.EAP@chiesi.com | |
| Clinical Trials | Contact | clinicaltrials_info@chiesi.com |
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| ID | Term |
|---|---|
| D008363 | alpha-Mannosidosis |
| ID | Term |
|---|---|
| D044904 | Mannosidase Deficiency Diseases |
| D002239 | Carbohydrate Metabolism, Inborn Errors |
| D008661 | Metabolism, Inborn Errors |
| D030342 | Genetic Diseases, Inborn |
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| D009358 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities |
| D016464 | Lysosomal Storage Diseases |
| D008659 | Metabolic Diseases |
| D009750 | Nutritional and Metabolic Diseases |