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Expanded Access Use of Itacitinib to Treat a Single Patient With Aplastic Anemia
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| Name | Type | Description | Arm Group Labels | Other Names |
|---|---|---|---|---|
| Iticitinib | Drug |
Inclusion Criteria:
-
Exclusion Criteria:
-
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| Name | Affiliation | Role |
|---|---|---|
| Lisa Forbes Satter, MD | Baylor College of Medicine | Principal Investigator |
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| PubMed Identifier | Type | Citation | Retractions |
|---|---|---|---|
| 35590143 | Derived | Rosenberg JM, Peters JM, Hughes T, Lareau CA, Ludwig LS, Massoth LR, Austin-Tse C, Rehm HL, Bryson B, Chen YB, Regev A, Shalek AK, Fortune SM, Sykes DB. JAK inhibition in a patient with a STAT1 gain-of-function variant reveals STAT1 dysregulation as a common feature of aplastic anemia. Med. 2022 Jan 14;3(1):42-57.e5. doi: 10.1016/j.medj.2021.12.003. |
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| ID | Term |
|---|---|
| D000741 | Anemia, Aplastic |
| ID | Term |
|---|---|
| D000740 | Anemia |
| D006402 | Hematologic Diseases |
| D006425 | Hemic and Lymphatic Diseases |
| D000080983 | Bone Marrow Failure Disorders |
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| D001855 | Bone Marrow Diseases |