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This is a long-term, multi-center, longitudinal, observational study in children with achondroplasia (ACH). The aim is to study height velocity and comorbidities in children with ACH. This is a natural history study and no study medication will be administered.
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| Measure | Description | Time Frame |
|---|---|---|
| Annualized height velocity (centimeters/year) in children with achondroplasia | Subjects will undergo a series of height measurements (in centimeters) on Day 1 and then every 6 months over the study period with height velocity reported in cm/year | Up to 5 years |
| Measure | Description | Time Frame |
|---|---|---|
| Collection of natural history of achondroplasia symptoms in children with achondroplasia | To characterize achondroplasia symptoms in children with achondroplasia | Up to 5 years |
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Inclusion Criteria:
Exclusion Criteria:
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Infants and children with achondroplasia from birth to 8 years of age.
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| Facility | Status | City | State | ZIP | Country | Contacts |
|---|---|---|---|---|---|---|
| Ascendis Pharma Investigational Site | Little Rock | Arkansas | 72211 | United States | ||
| Ascendis Pharma Investigational Site |
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| Oakland |
| California |
| 94609 |
| United States |
| Ascendis Pharma Investigational Site | Aurora | Colorado | 80045 | United States |
| Ascendis Pharma Investigational Site | Wilmington | Delaware | 19803 | United States |
| Ascendis Pharma Investigational Site | Saint Paul | Minnesota | 55102 | United States |
| Ascendis Pharma Investigational Site | Columbia | Missouri | 65212 | United States |
| Ascendis Pharma Investigational Site | Buffalo | New York | 14203 | United States |
| Ascendis Pharma Investigational Site | Houston | Texas | 77030 | United States |
| Ascendis Pharma Investigational Site | Seattle | Washington | 98105 | United States |
| Ascendis Pharma Investigational Site | Madison | Wisconsin | 53705 | United States |
| Ascendis Pharma Investigational Site | Parkville | Victoria | 3052 | Australia |
| Ascendis Pharma Investigational Site | Linz | 4020 | Austria |
| Ascendis Pharma Investigational Site | Edmonton | Alberta | T6G-1C9 | Canada |
| Ascendis Pharma Investigational Site | Ottawa | Ontario | 51H 8L1 | Canada |
| Ascendis Pharma Investigational Site | Montreal | Quebec | H3T 1C5 | Canada |
| Ascendis Pharma Investigational Site | Beijing | 100045 | China |
| Ascendis Pharma Investigational Site | Guangzhou | 510080 | China |
| Ascendis Pharma Investigational Site | Hangzhou | 310053 | China |
| Ascendis Pharma Investigational Site | Shanghai | 20082 | China |
| Ascendis Pharma Investigational Site | Shenzhen | 518053 | China |
| Ascendis Pharma Investigational Site | Wuhan | 430030 | China |
| Ascendis Pharma Investigational Site | Copenhagen | Capital Region | 2100 | Denmark |
| Ascendis Pharma Investigational Site | Paris | 75743 | France |
| Ascendis Pharma Investigational Site | Berlin | 13353 | Germany |
| Ascendis Pharma Investigational Site | Dublin | 1 | Ireland |
| Ascendis Pharma Investigational Site | Milan | 20132 | Italy |
| Ascendis Pharma Investigational Site | Auckland | 1142 | New Zealand |
| Ascendis Pharma Investigational Site | Coimbra | 3000 | Portugal |
| Ascendis Pharma Investigational Site | Barcelona | 08035 | Spain |
| Ascendis Pharma Investigational Site | Esplugues de Llobregat | 8950 | Spain |
| Ascendis Pharma Investigational Site | Madrid | 28046 | Spain |
| Ascendis Pharma Investigational Site | Vitoria-Gasteiz | 1008 | Spain |
| Ascendis Pharma Investigational Site | Lausanne | 1005 | Switzerland |
| Ascendis Pharma Investigational Site | Glasgow | G51 4TF | United Kingdom |
| Ascendis Pharma Investigational Site | London | SE1 7EU | United Kingdom |
| ID | Term |
|---|---|
| D000130 | Achondroplasia |
| D004392 | Dwarfism |
| ID | Term |
|---|---|
| D001848 | Bone Diseases, Developmental |
| D001847 | Bone Diseases |
| D009140 | Musculoskeletal Diseases |
| D010009 | Osteochondrodysplasias |
| D030342 | Genetic Diseases, Inborn |
| D009358 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities |
| D004700 | Endocrine System Diseases |
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