Expanded access may be provided for qualified patients who have limited treatment options and are not eligible for a clinical trial.
Long Chain Fatty Acid Oxidation Disorders (LC-FAOD) and other Non-FAOD conditions, where applicable: Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies.
For full details, please visit the links provided below.
- The participant must not be eligible for a UX007 clinical trial
EarlyAccess@ultragenyx.com