A Randomized, Double Blind, Placebo-Controlled, Study to Assess the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy
A Randomized, Double Blind, Placebo-Controlled, Study to Assess the Efficacy, Safety, and Tolerability of RO7239361 in Ambulatory Boys With Duchenne Muscular Dystrophy
This is a multi-center, randomized, double-blind, placebo-controlled study to assess the efficacy, safety and tolerability of two different weekly doses of RO7239361 in ambulatory boys with Duchenne Muscular Dystrophy (DMD).
Inclusion Criteria:
Exclusion Criteria:
Other protocol defined Inclusion/Exclusion Criteria could apply.
New Haven, Connecticut 06510, United States
Worcester, Massachusetts 01655, United States
Cincinnati, Ohio 45229, United States
Columbus, Ohio 43205, United States
South Brisbane, Queensland 4101, Australia
Paris, 75571, France
Milano, Emilia-Romagna 20162, Italy
Messina, Sicily 98125, Italy
Esplugues de Llobregas, Barcelona 08950, Spain