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The purpose of this study is to evaluate the long-term safety, efficacy, and pharmacokinetics of KPS-0373 in SCD patients
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| Label | Type | Description | Intervention Names |
|---|---|---|---|
| KPS-0373 | Experimental |
|
| Name | Type | Description | Arm Group Labels | Other Names |
|---|---|---|---|---|
| KPS-0373, High dose | Drug |
| ||
| KPS-0373, Low dose |
| Measure | Description | Time Frame |
|---|---|---|
| SARA (Scale for the Assessment and Rating of Ataxia) | 52 weeks |
| Measure | Description | Time Frame |
|---|---|---|
| SF-8 (QOL) | 52 weeks |
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Inclusion Criteria:
Exclusion Criteria:
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| Facility | Status | City | State | ZIP | Country | Contacts |
|---|---|---|---|---|---|---|
| Tokyo and Other Japanese Cities | Japan |
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| ID | Term |
|---|---|
| D013132 | Spinocerebellar Degenerations |
| D020754 | Spinocerebellar Ataxias |
| ID | Term |
|---|---|
| D002526 | Cerebellar Diseases |
| D001927 | Brain Diseases |
| D002493 | Central Nervous System Diseases |
| D009422 | Nervous System Diseases |
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|
| D013118 | Spinal Cord Diseases |
| D020271 | Heredodegenerative Disorders, Nervous System |
| D019636 | Neurodegenerative Diseases |
| D030342 | Genetic Diseases, Inborn |
| D009358 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities |
| D002524 | Cerebellar Ataxia |
| D001259 | Ataxia |
| D020820 | Dyskinesias |
| D009461 | Neurologic Manifestations |