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This is a single patient compassionate use protocol to determine whether Buphenyl (4-phenylbutyrate) will improve the poor bile flow associated with Byler Disease.
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| Name | Type | Description | Arm Group Labels | Other Names |
|---|---|---|---|---|
| Buphenyl | Drug |
Inclusion Criteria:
Exclusion Criteria:
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| ID | Term |
|---|---|
| C535933 | Cholestasis, progressive familial intrahepatic 1 |
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| ID | Term |
|---|---|
| C075773 | 4-phenylbutyric acid |
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