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The primary objective is to provide access to eculizumab for PNH patient pending commercial availability.
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| Name | Type | Description | Arm Group Labels | Other Names |
|---|---|---|---|---|
| eculizumab | Drug | 600mg IV every week and 900mg IV every 2 weeks |
Inclusion Criteria:
Exclusion Criteria:
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| Facility | Status | City | State | ZIP | Country | Contacts |
|---|---|---|---|---|---|---|
| Anthony Botti | Livingston | New Jersey | United States |
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| ID | Term |
|---|---|
| D006457 | Hemoglobinuria, Paroxysmal |
| ID | Term |
|---|---|
| D000743 | Anemia, Hemolytic |
| D000740 | Anemia |
| D006402 | Hematologic Diseases |
| D006425 | Hemic and Lymphatic Diseases |
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| ID | Term |
|---|---|
| C481642 | eculizumab |
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| D009190 |
| Myelodysplastic Syndromes |
| D001855 | Bone Marrow Diseases |